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Live-cel Technology

Team

News

Live-cel Technology

Team

News

Live-cel Technology

Team

News

Video Presentation Aug 2025 (9 minutes)

Glafabra Therapeutics — The re-administrable, non-myeloablative cell-based gene therapy for lysosomal storage disorders.

FDA Orphan Drug Designation granted for GT-GLA-S03 | Pilot clinical trial complete (Canada) | U.S. IND target mid-2027

Live-cel is an investigational treatment. It is not approved by the FDA or Health Canada and is being developed for FDA-authorized clinical trial in US. Patients should speak with their Fabry specialist before making any treatment decisions.