Glafabra Granted Orphan Drug Designation

Rogue Funds Signs Commitment

Glafabra Q3 Update

Comparison of LVV to AAV and Abs

Stem Cell Therapy for Fabry Disease

Q2 Update 2025

Metabolic Enzyme Disorders

Options Agreement on Improved Lentivector

Partnership with University of Utah Health

Glafabra Welcomes Elizabeth Wagner to Advisory Board

New Fabry disease therapy shows 130x increase in effectiveness.